Emil Kakkis | |
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Born | 1960 |
Education | Pomona College UCLA David Geffen School of Medicine at UCLA |
Known for | Developing treatments for ultra rare disorders |
Medical career | |
Institutions | Ultragenyx Pharmaceutical Inc., Founder, CEO and President Kakkis EveryLife Foundation, Founder BioMarin, Former Chief Medical Officer |
Sub-specialties | Rare biochemical and genetic diseases also known as inborn errors of metabolism |
Research | Enzyme Replacement Therapy |
Awards | Bogen Prize Vaile Prize in Biology Lifetime achievement award from the National MPS Society California Life Sciences Award |
Emil Kakkis (born 1960) is an American medical geneticist known for his work to develop treatments for ultra rare disorders. He is the Founder of the Everylife Foundation for Rare Disease and Founder, CEO and President of Ultragenyx Pharmaceutical Inc.