Clinical data | |
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Trade names | Vyondys 53 |
Other names | SRP-4053 |
AHFS/Drugs.com | Monograph |
License data |
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Routes of administration | Intravenous |
Drug class | Antisense oligonucleotide |
ATC code | |
Legal status | |
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Identifiers | |
CAS Number | |
DrugBank | |
UNII | |
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Chemical and physical data | |
Formula | C305H481N138O112P25 |
Molar mass | 8647.401 g·mol−1 |
Golodirsen, sold under the brand name Vyondys 53, is a medication used for the treatment of Duchenne muscular dystrophy.[2] It is an antisense oligonucleotide medication of phosphorodiamidate morpholino oligomer (PMO) chemistry.[1][3]
The most common side effects include headache, fever, fall, cough, vomiting, abdominal pain, cold symptoms (nasopharyngitis) and nausea.[2][1]
FDA PR
was invoked but never defined (see the help page).